Module 8 : GENE THERAPY : INTRODUCTION AND METHODS

Lecture 1 : Gene Therapy: Introduction and Methods

Figure 8-1.5.2: Various steps of in vivo gene transfer

 

Table 8-1.5.1: Differences between In Vivo and Ex Vivo gene therapy

8-1.6 Target sites for Gene Therapy

Therapeutic genes have to be delivered to specific target sites for a specific type of disease. This table describes the list of such disease and their target sites for gene therapy.

Table 8-1.6.1: Target cells for gene transfer

8-1.7 Vectors for gene therapy

Vectors for gene therapy can be classified into two types:

1. Viral vectors

2. Non-viral